A series of aggregated randomized-controlled N-of-1 trials with mexiletine in non-dystrophic myotonia: clinical trial results and validation of rare disease design

Bas Stunnenberg, Joost Raaphorst, Hans Groenewoud, Jeffrey Statland, Robert Griggs, Willem Woertman, Dick Stegeman, Janneke Timmermans, Jaya Trivedi, Emma Matthews, Christiaan Saris, Bas Schouwenberg, Gea Drost, Baziel van Engelen, GertJan van der Wilt

Research output: Contribution to journalMeeting AbstractAcademic

Original languageEnglish
Number of pages3
JournalNeurology
Volume90
Publication statusPublished - 10-Apr-2018
Event70th Annual Meeting of the American-Academy-of-Neurology (AAN) - Los Angeles, Canada
Duration: 21-Apr-201827-Apr-2018

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