Analysis of long-term treatment effects of odevixibat on clinical outcomes in children with progressive familial intrahepatic cholestasis in odevixibat clinical studies vs external controls from the NAPPED database

  • Bettina Hansen
  • , Velichka Valcheva
  • , Qifeng Yu
  • , Daan van Wessel
  • , Richard Thompson
  • , Emmanuel Gonzalès
  • , Irena Jankowska
  • , Etienne Sokal
  • , Tassos Grammatikopoulos
  • , Agustina Kadaristiana
  • , Emmanuel Jacquemin
  • , Anne Spraul
  • , Patryk Lipiński
  • , Piotr Czubkowski
  • , Nathalie Rock
  • , Mohammad Shagrani
  • , Kishwer Kumar
  • , Fowzan Alkuraya
  • , Meddirevula Sateesh
  • , Dieter Clemens Broering
  • Emanuele Nicastro, Deirdre Kelly, Gabriella Nebbia, Henrik Arnell, Björn Fischler, Daniele Serranti, Cigdem Arıkan, Esra Polat, Dominique Debray, Florence Lacaille, Cristina Gonçalves, Loreto Hierro Llanillo, Gema Muñoz Bartolo, Yael Mozer-Glassberg, Amer Azaz, Jernej Brecelj, Antal Dezsőfi, Pier Luigi Calvo, Enke Grabhorn, Ekkehard Sturm, Wendy L. van der Woerd, Binita M. Kamath, Jian-She Wang, Li Liting, Ozlem Durmaz, Zerrin Önal, Antonia Felzen, Mark Nomden, Jaak Sonajalg, Philip Stein, Quanhong Ni, Henkjan Verkade

    Research output: Contribution to conferencePosterAcademic

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