Compositions and methods useful for treating diseases characterized by insufficient pantothenate kinase activity

Gregor Kosec, (Inventor), Ajda Podgorsek Berke (Inventor), Hrvoje Petkovic, (Inventor), Oda Cornelia Maria Sibon (Inventor), Balaji Srinivasan, (Inventor), Susan J. Hayflick (Inventor)

Research output: Patent


Methods and pharmaceutical compositions for use in treating diseases associated with insufficient activity of the pantothenate kinase enzyme (e.g., CASTOR diseases) are disclosed. The methods and compositions involve an effective amount of an active derivative of 4'-phosphopantetheine.

Original languageEnglish
Patent numberWO2017218963
Priority date16/06/2016
Publication statusPublished - 21-Dec-2017

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