Original language | English |
---|---|
Pages (from-to) | A51-A51 |
Number of pages | 1 |
Journal | Human Gene Therapy |
Volume | 32 |
Issue number | 19-20 |
Publication status | Published - Oct-2021 |
Dose dependent lowering of alpha-synuclein and rescue of motor phenotype by miRNA-based AAV gene therapy
S. A. Broekmans, C. V. Tornero, F. Akyol, L. Toonen, S. Kieper, K. E. Ronde, W. Hogewerf, E. D. Tolsma, R. I. Seinstra, L. L. S. Janssen, E. A. A. Nolen, A. Valles
Research output: Contribution to journal › Meeting Abstract › Academic