Dose dependent lowering of alpha-synuclein and rescue of motor phenotype by miRNA-based AAV gene therapy

S. A. Broekmans, C. V. Tornero, F. Akyol, L. Toonen, S. Kieper, K. E. Ronde, W. Hogewerf, E. D. Tolsma, R. I. Seinstra, L. L. S. Janssen, E. A. A. Nolen, A. Valles

    Research output: Contribution to journalMeeting AbstractAcademic

    Original languageEnglish
    Pages (from-to)A51-A51
    Number of pages1
    JournalHuman Gene Therapy
    Volume32
    Issue number19-20
    Publication statusPublished - Oct-2021

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