Pharmacokinetics and pharmacodynamics of PTC518, an oral huntingtin lowering splicing modifier: A first-in-human study

  • Lan Gao
  • , Anuradha Bhattacharyya
  • , Brian Beers
  • , Diksha Kaushik
  • , Amy Lee Bredlau
  • , Allan Kristensen
  • , Khalid Abd-Elaziz
  • , Richard Grant
  • , Lee Golden
  • , Ronald Kong*
    • *Corresponding author for this work

    Research output: Contribution to journal › Article › Academic › peer-review

    6 Citations (Scopus)
    80 Downloads (Pure)

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    Keyphrases

    Pharmacology, Toxicology and Pharmaceutical Science