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The present invention relates to the use of compounds of formula (I) as inhibitors of RNA guided endonucleases, e.g., Cas9 and Cpfl, and methods for the inhibition of the function of such RNA guided endonucleases, including their use in the treatment and prevention of conditions or diseases.

Original languageEnglish
Patent numberWO2021198275
Priority date30/03/2020
Filing date30/03/2021
Publication statusPublished - 7-Oct-2021


  • CRISPR Cas9


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