Samenvatting
Methods and pharmaceutical compositions for use in treating diseases associated with insufficient activity of the pantothenate kinase enzyme (e.g., CASTOR diseases) are disclosed. The methods and compositions involve an effective amount of an active derivative of 4'-phosphopantetheine.
Originele taal-2 | English |
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Octrooinummer | WO2017218963 |
Prioriteitsdatum | 16/06/2016 |
Status | Published - 21-dec.-2017 |